WSJ Health Blog Reports – Results in Mice May Help Shape Clinical Trial for Children With Rare Fatal Disease
By Amy Dockser Marcus, Wall Street Journal Health Blog It’s a well-known maxim in science that curing a disease in a rodent doesn’t guarantee the same results in a human being. But new research on using the drug cyclodextrin in mice is likely to help shape a clinical trial being planned for children with a [...]
Do We Need a War on Rare Diseases?
By Amy Dockser Marcus, Wall Street Journal Is it time to declare a national “war on rare diseases” comparable to the famous “war on cancer” that began in the 1970s? The Institute of Medicine report released today stops short of recommending a full martial assault, but it does call for the creation of an aggressive [...]
Increased Patient Participarticipation in the Fight Against Rare Disease
The Institute of Medicine (IOM) issued a new report: “Rare Diseases and Orphan Products: Accelerating Research and Development” which calls for increased participarticipation by people with rare diseases.
FDA Database Aims to Spark Orphan-Disease Drug Development
By Amy Dockser Marcus For months now, the Food and Drug Administration has been trying novel ways of encouraging drug makers to develop drugs for rare diseases. Today the agency’s Office of Orphan Products Development is launching a new gambit—a database of FDA-approved compounds and products that show promise in rare diseases too. The concept [...]
Sharing information moves science ahead.
Short article on scientists and the sharing of information/collaboration, by Amy Dockser Marcus of the Wall Street Journal, link here, definitely something you should read today. (Thank you “Where are the Cures” Facebook page updates for the heads up.) :: Catherine C. Recommend on Facebook Share on Linkedin share via Reddit Share with Stumblers Tweet [...]