The Tour de France and Testicular Cancer
Testicular cancer is rare, and bone marrow transplant services are difficult to access for advanced stage tumors.
FDA and Rare Disease Drug Development, from FDA Week
June 29, 2010 // [FDA Week, http://insidehealthpolicy.com/] FDA is currently in the middle of a flurry of activity aimed at better focusing its regulation of rare disease treatments, but the agency disappointed some outside advocates by delaying the possibility of creating a special rare disease review division within FDA for at least a year. That [...]
FDA Hearing on Rare and Tropical (Neglected) Diseases
Just finished up watching the FDA hearing webcast from earlier this week. Loving Sen. Sam Brownback. If you have a rare disease, “God bless ya” because we “got no treatment for you.” The billion dollar per drug model doesn’t work for 7,000 rare diseases. We need a new different model – adjust the system so [...]