FasterCures

Wall Street Journal Reports – Do It Yourself Drug Development, With Some Help!

By nboice on December 27, 2011

The effort by two families to buy and develop a drug that holds promise in treating Duchenne muscular dystrophy — described today in the WSJ — is the result of an innovative new model set up to support the burgeoning phenomenon of do-it-yourself drug development. Before the Seckler and Wicka families bought halofuginone, a drug that [...]

Posted in Advocacy/Policy, Bench to Bedside, Featured, Global Community, News | Tagged Charley's Fund, Dart Therapeutics, Duchenne Muscular Dystrophy, Eugene Williams, FasterCures, FDA, Food and Drug Administration, Genzyme, Halo Therapeutics, orphan drug development, orphan drugs, Rare Disease, rare disorders, Wall Street Journal | 1 Response

'Denim Jean' Ribbon Unveiled To Promote Rare Disease Awareness

By nboice on February 1, 2010

Campaign Brings Together Support from over 90 Corporations, Non-Profit Foundations, Research Institutions, Hospitals and Advocacy Groups; New Blue Jeans Denim Ribbon Unveiled To Promote Rare Disease Awareness DANA POINT, CA – February 1, 2010 – Hope – It’s In Our Genes.™ The Children’s Rare Disease Network today announced the Global Genes Project, an initiative designed [...]

Posted in Featured, Global Community, Global Genes Project, News | Tagged 23andMe, Amicus Therapeutics, Better Health, BioMarin, CheckOrphan, Children, children wtih rare disease, childrens rare disease network, CollabRx, Coriell Institute, Counsyl, denim ribbon, DonateGames.org, FasterCures, FreeForm, genetic alliance, Geni.com, Genzyme, Global Genes Project, hide and seek foundation, Jackson Laboratory, Kakkis EveryLife Foundation, Knome, Life Technologies, Lili Claire Foundation, Mayo Clinic and Shire, NIH, Orphan Drug Act, Public Health, Rare Disease, rare disorders, therapy development, World Rare Disease Day | Leave a response

FasterCures

Wall Street Journal Reports – Do It Yourself Drug Development, With Some Help!

'Denim Jean' Ribbon Unveiled To Promote Rare Disease Awareness

THE DISEASE MAY BE RARE, BUT HOPE SHOULD NOT BE

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